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Gene therapy helps diagnose, treat and prevent disease. It treats disease by replacing or correcting disease-causing genes of patients with particular life threatening genetic disorders. Gene therapy is best suited for single enzyme deficiency diseases such as severe combined immunodeficiency also known as SCID and has often been called ‘baby in a bubble’ syndrome due to the sterile conditions the patient must live in to avoid contracting a deadly infection. The defining feature of SCID is a fault in the white blood cells B- and T-lymphocytes. This results in the non fu